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Ultragenyx Pharmaceutical Inc. (RARE) Stock Analysis

SellModerate Confidence

Healthcare · Biotechnology

Earnings in 5 days (2026-05-05). Expect elevated volatility around the report — consider waiting for post-earnings price action before new entries.

Sell if holding. Engine safety override at $25.00: a dimension score below its floor triggers a hard block regardless of the otherwise-positive setup — overall score 5.4/10 and A.R:R 6.1:1 is above the 1.5:1 BUY gate. Specifically: High short interest: 13%; Elevated put/call ratio: 1.38; Below-average business quality.

Ultragenyx is a biopharmaceutical company with approved therapies Crysvita (XLH/TIO), Mepsevii (MPS VII), and others for rare/ultra-rare genetic diseases. Revenue comes from product sales and collaborations, notably with Kyowa Kirin (KKC) for Crysvita global commercialization;... Read more

$25.00+92.2% A.UpsideScore 5.4/10#46 of 158 Biotechnology
Stop $23.24Target $48.02(analyst − 10%)A.R:R 6.1:1
Analyst target$53.35+113.4%20 analysts
$48.02our TP
$25.00price
$53.35mean
$84

Sell if holding. Engine safety override at $25.00: a dimension score below its floor triggers a hard block regardless of the otherwise-positive setup — overall score 5.4/10 and A.R:R 6.1:1 is above the 1.5:1 BUY gate. Specifically: High short interest: 13%; Elevated put/call ratio: 1.38; Below-average business quality. Chart setup: No recognized chart pattern (not a breakout, bounce, continuation, recovery, falling knife, or range) — technicals mixed. Score 5.4/10, moderate confidence.

Passes 4/7 gates (favorable risk/reward ratio, clean insider activity, no SEC red flags, semi cycle peak clear). Fails on weak momentum and death cross (50MA < 200MA) and earnings proximity 5d<=7d. Suitability: aggressive.

Thesis

Rewards
No bull case signals
Risks
Concentration risk — Supplier: KKC
Concentration risk — Supplier: single-source suppliers
Quality below floor (2.5 < 4.0)

Key Metrics

P/E (TTM)
P/E (Fwd)-1899.5
Mkt Cap$2.4B
EV/EBITDA-5.8
Profit Mgn-85.4%
ROE-608.5%
Rev Growth25.9%
Beta0.25
DividendNone
Rating analysts26

Quality Signals

Piotroski F4/9

Options Flow

P/C1.38bearish
IV80%elevated
Max Pain$43+70.0% vs spot

Concentration Risks(10-K Item 1A)

  • HIGHSupplierKKC
    10-K Item 1A: 'We are dependent on KKC for the supply and commercialization of Crysvita in certain major markets.'
  • HIGHSuppliersingle-source suppliers
    10-K Item 1A: 'The failure to supply by any of our single-source suppliers could adversely affect our business.'

Material Events(8-K, last 90d)

  • 2026-02-12Item 2.05MEDIUM
    Ultragenyx announced strategic restructuring: 10% workforce reduction (~130 employees) beginning Feb 12, 2026, substantially complete in H1 2026. Total charges ~$50M including ~$40M for termination of UX143 manufacturing agreements.
    SEC filing →

Model-generated analysis — not investment advice. Not a registered investment advisor. Past performance does not guarantee future results. Full disclaimer

Rating Breakdown

4 floor-breakers·2 ceiling hits

Clinical-stage biotech: losses expected pre-commercialisation. Quality floor doesn't distinguish R&D investment from operational decay — components above tell the real story.static

Roa
0.0
Operating Margin
0.0
Net Margin
0.0
Fcf Quality
0.0
Piotroski F
4.4
Moat
5.0
Current Ratio
8.4
Cash-burning: FCF -37% of revenueNo competitive moatQuality concerns

Technicals below the gate floor. Component breakdown shows what dragged the score down.static

52w Position
1.8
Bollinger
2.0
Support Resistance
2.2
Gap
5.0

Momentum below the gate floor. Component breakdown shows what dragged the score down.static

Volume
0.0
Obv
1.0
Rsi
3.8
Macd
3.8
Ma Position
6.0
Volume distribution (falling OBV)Below 200-MA, MA slope -6.9%/30d — confirmed downtrend

No near-term catalyst priced in. Thesis progression will come from fundamentals grinding, not event reaction.static

Surprise Avg
0.0
Earnings History
3.3
Erm
5.0
Earnings Timing
5.0
News Activity
5.0
Earnings concerns: 2B/2MEarnings in 5 days
GatesMomentum 2.9<4.5Death cross (50MA < 200MA)EARNINGS PROXIMITY 5d<=7dA.R:R 6.1 ≥ 1.5Insider activity: OKNo SEC red flagsSEMI CYCLE PEAK CLEARSuitability: Aggressive
RSI
62 · Neutral
20D MA 50D MA 200D MADEATH CROSSSupport $20.79Resistance $26.19

Price Targets

$23
$48
A.Upside+92.1%
A.R:R6.1:1

Position Sizing

ConvictionNone
Suggested %0.5%
Max %1%
RegimeSteady

Risk Alerts

! Quality below floor (2.5 < 4.0)
! Momentum score 2.9/10 — below 4.5 minimum
! Death cross — 50-day MA below 200-day MA

Earnings

B
B
M
M
2/4 beats
Next Earnings2026-05-05 (5d)

Verdict History

reverse chrono — latest first
Loading history...
Verdicts are recorded on every nightly pipeline run. Rows capture transitions (verdict flips, score deltas ≥0.3, entry/TP/SL changes). Rows with a ▶ can be expanded to see the change reason. Aggregate cohort performance is tracked in the recommendation ledger.
Frequently Asked Questions
Is RARE stock a buy right now?

Sell if holding. Engine safety override at $25.00: a dimension score below its floor triggers a hard block regardless of the otherwise-positive setup — overall score 5.4/10 and A.R:R 6.1:1 is above the 1.5:1 BUY gate. Specifically: High short interest: 13%; Elevated put/call ratio: 1.38; Below-average business quality. Chart setup: No recognized chart pattern (not a breakout, bounce, continuation, recovery, falling knife, or range) — technicals mixed. Prior stop was $23.24. Score 5.4/10, moderate confidence.

What is the RARE stock price target?

Take-profit target: $48.02 (+92.2% upside). Prior stop was $23.24. Stop-loss: $23.24.

What are the risks of investing in RARE?

Concentration risk — Supplier: KKC; Concentration risk — Supplier: single-source suppliers; Quality below floor (2.5 < 4.0).

Is RARE overvalued or undervalued?

Ultragenyx Pharmaceutical Inc. trades at a P/E of N/A (forward -1899.5). TrendMatrix value score: 8.6/10. Verdict: Sell.

What do analysts say about RARE?

26 analysts cover RARE with a consensus score of 4.2/5. Average price target: $53.

What does Ultragenyx Pharmaceutical Inc. do?Ultragenyx is a biopharmaceutical company with approved therapies Crysvita (XLH/TIO), Mepsevii (MPS VII), and others...

Ultragenyx is a biopharmaceutical company with approved therapies Crysvita (XLH/TIO), Mepsevii (MPS VII), and others for rare/ultra-rare genetic diseases. Revenue comes from product sales and collaborations, notably with Kyowa Kirin (KKC) for Crysvita global commercialization; available cash was $737M as of December 31, 2025.

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